Edgewise Therapeutics, Inc. (Nasdaq: EWTX), a leading muscle disease biopharmaceutical company, today presented at the 2026 ...

Precision BioSciences, Inc. (Nasdaq: DTIL), a clinical stage gene editing company utilizing its novel proprietary ARCUS® platform to develop in vivo gene editing therapies for high unmet need diseases ...

Planned submission for U.S. Accelerated Approval of z-rostudirsen on track for Q2 2026; potential launch in Q1 2027 -- Positive topline results ...

Background Becker muscular dystrophy (BMD) is a rare X-linked neuromuscular disorder predominantly affecting males. While respiratory function has been characterised in small cohorts over limited time ...

USA: Researchers have found in a new study that among people with cystic fibrosis (pwCF), handgrip strength (HGS) is associated with inspiratory muscle strength and percent-predicted forced vital ...

The federal statistical system is facing “unprecedented strain, uncertainty and transformation” in the face of staffing losses, funding pressures and threats to statistical integrity, according to a ...

Chelsea Rae Bourgeois is a health writer and registered dietitian nutritionist with over eight years of experience in the clinical setting. Her writing covers nutrition and overall health topics, ...

Avidity Biosciences, Inc. (NASDAQ:RNA) on Wednesday shared new data from participants treated continuously with del-zota for one year in the EXPLORE44 and EXPLORE44-OLE trials for Duchenne muscular ...

Participants aged 2 to 12 years receiving apitegromab had significantly higher improvements in motor function vs placebo. HealthDay News — For patients with nonambulatory type 2 or type 3 spinal ...

The least-squares mean difference in the Hammersmith Functional Motor Scale-Expanded change from baseline at 12 months was 1.8 points for those 2 to 12 years receiving apitegromab vs placebo.

Significant improvement seen in motor function for patients in combined 20- and 10-mg/kg dose groups vs placebo group. HealthDay News — For patients with nonambulatory type 2 or type 3 spinal muscular ...

Many diseases affect men and women differently. Asthma tends to strike men earlier in life, yet more women develop asthma as they get older. Parkinson's is more common in men, but Alzheimer's is more ...